Article

Adaptive Machine Learning Framework enables Unprecedented Yield and Purity of Adeno-Associated Viral Vectors for Gene Therapy

2025-05-24

Abstract excerpt

Adeno-associated viral (AAV) vectors for gene therapy are becoming integral to modern medicine, providing therapeutic options for diseases once deemed incurable. Currently, optimizing viral vector purification is a critical bottleneck in the gene therapy industry, impacting product efficacy and safety as well as accessibility and cost to patients. Traditional optimization methods are resource-intensive and often f...

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Literature Corpus work: 187280c1-ee0b-5966-8cc8-b2200007d7e5
DOI: 10.1101/2025.05.23.655859

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