Article

Identification of AAV serotypes for lung gene therapy in human embryonic stem cell derived lung organoids.

2020-07-09

Abstract excerpt

<title>Abstract</title> <p>Gene therapy is being investigated for a range of serious lung diseases, such as cystic fibrosis and emphysema. Recombinant adeno-associated virus (rAAV) is a well-established, safe, viral-vector for gene delivery with multiple natural and artificial serotypes available displaying alternate cell, tissue and species-specific tropisms. Efficient AAV serotypes for the transduction of the c...

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Literature Corpus work: d4e8a76a-4ea9-5d7a-ac86-5c7ca2bcf0e2
DOI: 10.21203/rs.3.rs-40720/v1

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