Article

Muscular dystrophy cell therapy : an in utero approach using human fetal mesenchymal stem cells

2009-01-01

Abstract excerpt

Duchenne muscular dystrophy (DMD) is the most prevalent genetic neuromuscular disorder and affects 1 in 3,500 live male births. Lack of the protein dystrophin in muscle fibres causes permanent muscle damage, is lethal and despite various potential therapeutic strategies aimed at restoring dystrophin expression, has no cure. As DMD affects all skeletal muscles as well as the heart, a systemic treatment would be nec...

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Literature Corpus work: b51ab7dc-c434-5e00-a181-3dc66b1127b4
DOI: 10.25560/4726

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