Article

Targeted Gene and Genome Editing Strategies for Epilepsy: Advances and Translational Challenges

2026-02-11

Abstract excerpt

Epilepsy affects more than 50 million individuals worldwide, and approximately one-third of patients remain refractory to existing antiseizure medications. Advances in gene therapy and genome editing have opened new possibilities for disease-modifying interventions that directly target the molecular and circuit-level mechanisms underlying epileptogenesis. Recent progress in central nervous system tropic viral vect...

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Literature Corpus work: af66a2fb-f901-5f72-841a-65974517df21
DOI: 10.20944/preprints202602.0886.v1

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