Article

Safety and tolerability of intravenous liposomal GM1 in patients with Parkinson disease: A single center open-label clinical phase I trial (NEON trial)

2024-09-06

Abstract excerpt

<h4>ABSTRACT</h4> <h4>Background:</h4> Parkinson disease (PD) is a chronic progressive neurodegenerative disorder leading to motor and non- motor impairment often resulting in severe loss of quality of life. There are symptomatic treatments without effect on the progression of PD. A disease-modifying treatment that could ideally stop the neurodegenerative process is direly needed. Monosialotetrahexosylganglioside...

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Literature Corpus work: 4b5cf50d-f124-5543-8018-4ed2d348a535
DOI: 10.1101/2024.09.05.24313105

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