Article

A Phase 2A randomized, double-blind, placebo-controlled pilot trial of GM604 in patients with Amyotrophic Lateral Sclerosis (ALS Protocol GALS-001) and a single compassionate patient treatment (Protocol GALS-C)

2017-03-07

Abstract excerpt

<h4>Background: </h4> Amyotrophic lateral sclerosis (ALS) is a fatal neurodegenerative disease that lacks effective treatment options. Genervon has discovered and developed GM604 (GM6) as a potential ALS therapy. GM6 has been modeled upon an insulin receptor tyrosine kinase binding motoneuronotrophic factor within the developing central nervous system. <ns4:p/> <h4>Methods: </h4> This was a 2-center phase 2A, ran...

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Literature Corpus work: a64f5537-63dd-5adc-ab9c-495ab2f6e62c
DOI: 10.12688/f1000research.10519.1

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