Improving the therapeutic efficacy of gene therapy for duchenne muscular dystrophy (DMD) by evaluating and managing inflammation

Abstract excerpt

Duchenne muscular dystrophy (DMD): is a rare, life-limiting genetic disorder for which no curative treatment currently exists. While various gene therapy approaches, some approved and others still under clinical investigation have been explored, they have not consistently produced the desired outcome and, in some cases, have been associated with serious adverse effects, including mortality. A critical factor we...

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