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Article

Current and Emerging Therapeutic Strategies for the Treatment of Duchenne Muscular Dystrophy.

Genes - 30 Apr 2026

Lopez Perez Miguel A, Weisleder Noah L

Abstract excerpt

Background/Objectives: Duchenne muscular dystrophy (DMD) is a fatal, progressive neuromuscular disorder caused by mutations in the dystrophin gene, leading to the absence of functional dystrophin protein. As the largest gene in the human genome, the DMD locus is highly susceptible to mutations, contributing to a prevalence of approximately 1 in 3800-6300 live male births worldwide. This review aims to provide a...

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Source

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Identifiers

PMID: 42194990
DOI: 10.3390/genes17050533
PMCID: PMC13205412

Genes

DMD

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 8 Sept 2026.

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