Discover Community Create You

Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Progress and prospects of gene therapy clinical trials for the muscular dystrophies

8 Oct 2015

Abstract excerpt

Clinical trials represent a critical avenue for new treatment development, where early phases (I, I/II) are designed to test safety and effectiveness of new therapeutics or diagnostic indicators. A number of recent advances have spurred renewed optimism toward initiating clinical trials and developing refined therapies for the muscular dystrophies (MD's) and other myogenic disorders. MD's encompass a...

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to CAR-T cell therapy research
Share to Muscle Physiology and Disorders
Share to Virus-based gene therapy research

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Source

Identifiers

PMID: 26450518
DOI: 10.1093/hmg/ddv420

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 8 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Progress and prospects of gene therapy clinical trials for the muscular dystrophiesPMID 26450518Read ↗

Towards a Cure: Emerging Therapeutic Advances for DMD, LGMD, and GNEM- Insights from Pre-Clinical and Clinical ResearchSemantic proximity Read ↗

Progress toward Gene Therapy for Duchenne Muscular Dystrophy.Semantic proximity Read ↗

Gene therapy for Duchenne muscular dystrophy: an update on the latest clinical developments.Semantic proximity Read ↗

Muscular dystrophy: new challenges and review of the current clinical trials.Semantic proximity Read ↗

Gene replacement therapies for duchenne muscular dystrophy using adeno-associated viral vectors.Semantic proximity Read ↗

Unmet Needs and Evolving Treatment for Limb Girdle Muscular DystrophiesSemantic proximity Read ↗

Current Clinical Applications of In Vivo Gene Therapy with AAVsSemantic proximity Read ↗

Therapeutic approaches for Duchenne muscular dystrophy.Semantic proximity Read ↗

Duchenne Muscular Dystrophy: From Diagnosis to Therapy.Semantic proximity Read ↗

The DMD gene and therapeutic approaches to restore dystrophin.Semantic proximity Read ↗

Molecular treatments in Duchenne muscular dystrophy.Semantic proximity Read ↗

Genetic treatments in muscular dystrophies.Semantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.