Back to search

Article

Towards a Cure: Emerging Therapeutic Advances for DMD, LGMD, and GNEM- Insights from Pre-Clinical and Clinical Research

2025-12-15

Abstract excerpt

Duchenne muscular dystrophy (DMD), Limb-girdle muscular dystrophies (LGMD), and GNE myopathy (GNEM) are progressive neuromuscular rare genetic diseases with differing etiologies either due to defects in structural muscle proteins or impaired metabolism and manifests through progressive weakening and deterioration of skeletal muscle tissues. This review summarizes current and recent clinical trials worldwide, highl...

Topics

Open a Topic to create a Post that cites this publication.

Identifiers and source

Literature Corpus work
81f6a6f8-dcb0-5a61-91b5-5bb38bc36428
DOI
10.20944/preprints202512.1267.v1
Open publication

Related research

Semantic proximity does not establish scientific evidence.

Click a neighbor to travelStep 1 · 12 closest
Interactive article relationship graphSelect a related publication card to move it into the centre and load its closest explainable connections. Solid lines are source-backed structured connections. Dashed lines are semantic discovery signals and are not scientific evidence.
Towards a Cure: Emerging Therapeutic Advances for DMD, LGMD, and GNEM- Insights from Pre-Clinical and Clinical ResearchDOI 10.20944/preprints202512.1267.v1
Emerging therapeutic strategies in muscular dystrophy: an updated review on pathogenesis and treatment advances.Semantic proximity
An Overview of Recent Therapeutics Advances for Duchenne Muscular Dystrophy.Semantic proximity
Muscle and cardiac therapeutic strategies for Duchenne muscular dystrophy: past, present, and future.Semantic proximity
Muscular dystrophy: new challenges and review of the current clinical trials.Semantic proximity
Advances in the Treatment of Duchenne Muscular Dystrophy: New and Emerging PharmacotherapiesSemantic proximity
The DMD gene and therapeutic approaches to restore dystrophin.Semantic proximity
Drug development progress in duchenne muscular dystrophySemantic proximity
Progress and prospects of gene therapy clinical trials for the muscular dystrophiesSemantic proximity
Neurology Care, Diagnostics, and Emerging Therapies of the Patient With Duchenne Muscular DystrophySemantic proximity
Gene therapy for Duchenne muscular dystrophy: an update on the latest clinical developments.Semantic proximity
Duchenne muscular dystrophy: an updated review of common available therapiesSemantic proximity
Therapeutic approaches for Duchenne muscular dystrophy.Semantic proximity
Select a neighboring publication to make it the new centre.