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Article

Small molecule therapeutics to treat the β-globinopathies.

Current opinion in hematology - 1 May 2020

Yu Lei, Myers Greggory, Engel James D

Abstract excerpt

PURPOSE OF REVIEW: The current review focuses on recent insights into the development of small molecule therapeutics to treat the β-globinopathies. RECENT FINDINGS: Recent studies of fetal γ-globin gene regulation reveal multiple insights into how γ-globin gene reactivation may lead to novel treatment for β-globinopathies. SUMMARY: We summarize current information regarding the binding of transcription factors...

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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Source

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Identifiers

PMID: 32167945
DOI: 10.1097/MOH.0000000000000579
PMCID: PMC10916415

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 6 Sept 2026. Manifest publication-graph-cohort-2026-09-06.1.

Source receipt: pubmed, retrieved 6 Sept 2026.

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