Article

Atlas of CRISPR Correction of Pathogenic Human Genetic Variants

2025-03-25

Abstract excerpt

<title>Abstract</title> <p>Inherited genetic disorders impact at least 300 million individuals worldwide, presenting a significant therapeutic challenge. Although CRISPR-based genome editing offers a promising avenue for targeted interventions, the pathogenic and likely pathogenic variants amenable to such treatments have yet to be fully delineated. Here, we present the mEdit platform (https://igimedit.org) along...

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Literature Corpus work: f81de310-54f6-5fef-8adf-8d7b4071d021
DOI: 10.21203/rs.3.rs-6107416/v1

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