Article

Natural history of serum creatine kinase levels and motor, pulmonary, and cardiac functions in 337 patients with Duchenne muscular dystrophy: a retrospective study at a single referral center in Japan

2022-10-21

Abstract excerpt

<h4>Introduction/Aims</h4> Duchenne muscular dystrophy (DMD) presents with skeletal muscle weakness, followed by respiratory and cardiac muscle involvement. Recently, with the development of treatments, the need for a natural history to serve as a control for determining treatment efficacy in clinical trials has increased dramatically, however, few large-scale studies have investigated changes in these symptoms. T...

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Literature Corpus work: c8bb7414-10a9-509d-a864-9329ddaa3319
DOI: 10.1101/2022.10.19.22281246

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