Article

Comprehensive analysis of 2097 Patients with Dystrophinopathy Based on a Database From 2011 to 2021

2023-07-20

Abstract excerpt

<title>Abstract</title> <p>Background A growing number of clinical trials for new therapeutic strategies are being conducted or considered for dystrophinopathy. Detailed data on natural history will facilitate the evaluation of the effectiveness of new drugs for this rare disease. Nevertheless, there is a paucity of data regarding the long-term natural history and associated management in China. Here, we provide...

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Literature Corpus work: cbd9eb51-5f0e-5945-ba43-326bd20d684b
DOI: 10.21203/rs.3.rs-3146626/v1

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