Discover Community Create You

Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Therapeutic approaches for Duchenne muscular dystrophy.

Nature reviews. Drug discovery - 1 Nov 2023

Roberts Thomas C, Wood Matthew J A, Davies Kay E

Abstract excerpt

Duchenne muscular dystrophy (DMD) is a monogenic muscle-wasting disorder and a priority candidate for molecular and cellular therapeutics. Although rare, it is the most common inherited myopathy affecting children and so has been the focus of intense research activity. It is caused by mutations that disrupt production of the dystrophin protein, and a plethora of drug development approaches are under way that aim...

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to Child
Share to Codon, Terminator
Share to Dystrophin

Methodology Data sources Editorial policy Privacy Delete account & data About Contact Helena Bioinformatics

Share to Muscular Dystrophy, Duchenne

Share to Mutation

Share to Oligonucleotides, Antisense

Source

Identifiers

PMID: 37652974
DOI: 10.1038/s41573-023-00775-6

Genes

DMD

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-08.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence. Graph snapshot: 2026-09-29.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Therapeutic approaches for Duchenne muscular dystrophy.PMID 37652974Read ↗

Advances in the Treatment of Duchenne Muscular Dystrophy: New and Emerging PharmacotherapiesSemantic proximity Read ↗

Molecular treatments in Duchenne muscular dystrophy.Semantic proximity Read ↗

Gene therapy for Duchenne muscular dystrophy: an update on the latest clinical developments.Semantic proximity Read ↗

Exon-Skipping in Duchenne Muscular Dystrophy.Semantic proximity Read ↗

Developing DMD therapeutics: a review of the effectiveness of small molecules, stop-codon readthrough, dystrophin gene replacement, and exon-skipping therapies.Semantic proximity Read ↗

Recent Trends in Antisense Therapies for Duchenne muscular dystrophySemantic proximity Read ↗

Duchenne muscular dystrophy: an updated review of common available therapiesSemantic proximity Read ↗

Biological and genetic therapies for the treatment of Duchenne muscular dystrophy.Semantic proximity Read ↗

Current and Emerging Therapeutic Strategies for the Treatment of Duchenne Muscular Dystrophy.Semantic proximity Read ↗

The DMD gene and therapeutic approaches to restore dystrophin.Semantic proximity Read ↗

Brogidirsen and Exon 44 Skipping for Duchenne Muscular Dystrophy: Advances and Challenges in RNA-Based TherapySemantic proximity Read ↗

Muscular dystrophy: new challenges and review of the current clinical trials.Semantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.