Article
Muscle and cardiac therapeutic strategies for Duchenne muscular dystrophy: past, present, and future.
Pharmacological reports : PR - 1 Oct 2020
Łoboda Agnieszka, Dulak Józef
Abstract excerpt
BACKGROUND: Duchenne muscular dystrophy (DMD) is a severe X-linked neuromuscular childhood disorder that causes progressive muscle weakness and degeneration and results in functional decline, loss of ambulation and early death of young men due to cardiac or respiratory failure. Although the major cause of the disease has been known for many years-namely mutation in the DMD gene encoding dystrophin, one of the...
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