Article

Early economic evaluation of a predictive tool to test CFTR modulator treatment response in people with cystic fibrosis

2026-01-13

Abstract excerpt

<h4>Background</h4> Innovative treatments for rare diseases often strain healthcare budgets. Precision medicine can improve care and reduce costs by guiding treatment allocation. One example is the forskolin-induced swelling (FIS) assay, which uses patient-derived organoids to predict-response to Cystic Fibrosis Transmembrane conductance Regulator (CFTR) modulators in people with Cystic Fibrosis (pwCF). However,...

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Literature Corpus work: 0327316e-c1e8-5ae4-bbdb-a339d7a54d83
DOI: 10.64898/2026.01.12.26343787

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