Duchenne Muscular Dystrophy: Integrating Current Clinical Practice with Future Therapeutic and Diagnostic Horizons

Abstract excerpt

Duchenne Muscular Dystrophy (DMD) is a severe X-linked disorder characterized by progressive muscle degeneration due to mutations in the dystrophin gene. Despite major advancements in understanding its pathophysiology, there is still no curative treatment. This review provides an up-to-date overview of current and emerging therapeutic approaches— including antisense oligonucleotides, gene therapy, gene editing, co...

Topics

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• Adrenal Cortex Hormones
• Dependovirus
• Dystrophin
• Genetic Therapy
• Histone Deacetylase Inhibitors
• Muscle Physiology and Disorders
• Muscular Dystrophy, Duchenne
• Mutation

Identifiers and source

Literature Corpus work

ffeed6d9-da15-58be-b83b-af7d879362b7

DOI

10.20944/preprints202506.2161.v1