Article
Molecular treatments in Duchenne muscular dystrophy.
Current opinion in pharmacology - 1 Jun 2010
Guglieri Michela, Bushby Kate
Abstract excerpt
Duchenne muscular dystrophy (DMD) is the most common childhood muscular dystrophy and results from mutations in the dystrophin gene. Currently no treatment is available for this devastating condition. Standards of care have been improving and are spreading world-wide, prolonging survival and increasing quality of life, however management of symptoms and complications remains the only interventions that can...
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