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Article

Gene replacement therapies for duchenne muscular dystrophy using adeno-associated viral vectors.

Current gene therapy - 1 Jun 2012

Seto Jane T, Ramos Julian N, Muir Lindsey, Chamberlain Jeffrey S, Odom Guy L

Abstract excerpt

The muscular dystrophies collectively represent a major health challenge, as few significant treatment options currently exist for any of these disorders. Recent years have witnessed a proliferation of novel approaches to therapy, spanning increased testing of existing and new pharmaceuticals, DNA delivery (both anti-sense oligonucleotides and plasmid DNA), gene therapies and stem cell technologies. While none of...

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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Source

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Identifiers

PMID: 22533379
DOI: 10.2174/156652312800840603
PMCID: PMC4242712

Genes

DMD

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-07.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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