Article
Genetic treatments in muscular dystrophies.
Current opinion in neurology - 1 Oct 2007
Muntoni Francesco, Wells Dominic
Abstract excerpt
PURPOSE OF REVIEW: The search for a cure for Duchenne muscular dystrophy and other muscular dystrophies is progressing rapidly despite significant challenges posed by some genes and the complexity of targeting all skeletal muscles. This review focuses on three areas in which experimental clinical studies are in progress. RECENT FINDINGS: Two Phase I/IIa gene-therapy trials using adeno-associated viral vectors...
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