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Article

RNA repair: a novel approach to gene therapy.

Advanced drug delivery reviews - 15 Nov 2000

Watanabe T, Sullenger B A

Abstract excerpt

Treatment of genetic disorders by gene therapy has conventionally been attempted through the transfer of a wild type version of a gene to the cells of a patient harboring defective copies of a disease associated gene. Despite significant advances using this paradigm, several technical hurdles mus...

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Identifiers

PMID: 11072109
DOI: 10.1016/s0169-409x(00)00089-2

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 2 Sept 2026. Prepared record publication-11072109-2026-09-02.2. Manifest publication-graph-cohort-2026-09-02.2.

Source receipt: PubMed via Helena Literature Corpus, retrieved 2 Sept 2026.

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