Article

AAV-Txnip prolongs cone survival and vision in mouse models of retinitis pigmentosa

2021-01-27

Abstract excerpt

Retinitis pigmentosa (RP) is an inherited retinal disease, affecting >20 million people worldwide. Loss of daylight vision typically occurs due to the dysfunction/loss of cone photoreceptors, the cell type that initiates our color and high acuity vision. Currently, there is no effective treatment for RP, other than gene therapy for a limited number of specific disease genes. To develop a gene-agnostic therapy, we...

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Literature Corpus work: e9344e4b-4ea5-5bdc-b94f-3d94f4c3791d
DOI: 10.1101/2021.01.27.428411

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