Article

Treatment characteristics of patients with hereditary transthyretin amyloidosis: a cohort study

2023-10-04

Abstract excerpt

<title>Abstract</title> <p>Background There are novel medications approved for the treatment of hereditary transthyretin amyloidosis (ATTRv), classified as transthyretin (TTR) stabilizers or gene silencers. While many patients may be on both classes of medications, there is no data available on the safety and efficacy of combination therapy. Objectives To describe ATTRv patient and TTR-targeted therapy characte...

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Literature Corpus work: dcb6ce74-2c30-5534-abc5-628a25c72755
DOI: 10.21203/rs.3.rs-3221526/v1

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