Article

Therapeutic Applications of CRISPR-Cas9 Gene Editing

2025-10-10

Abstract excerpt

CRISPR-Cas9 is a gene editing tool used extensively in biological research that is now making its way into clinical therapies. With the first CRISPR therapy obtaining approval by the United States’ Food and Drug Administration (FDA) in late 2023, we look at clinical trials of emerging therapies involving CRISPR-Cas9, currently the most prevalent CRISPR-based tool in these trials. A CRISPR-based therapy is currentl...

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Literature Corpus work: d2e212e4-690f-516c-9f0f-ff2e8c67f273
DOI: 10.20944/preprints202510.0771.v1

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