Article

Development and validation of a high throughput screening platform to enable target identification in skeletal muscle cells from Duchenne Muscular Dystrophy (DMD) patients

2023-05-24

Abstract excerpt

<h4>ABSTRACT</h4> Duchenne muscular dystrophy (DMD) is a progressive and fatal muscle degenerating disease caused by dystrophin deficiency. Effective methods for drug discovery for the treatment of DMD requires systems to be physiologically relevant, scalable, and effective. To this end, the Myoscreen platform offers a scalable and physiologically relevant system for generating and characterizing patient-derived...

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Literature Corpus work: ab6c61e3-48b8-501d-bdb4-4e382956b814
DOI: 10.1101/2023.05.24.542079

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