Article

Identification of Adeno-Associated Virus Variants for Gene Transfer Into Human Neural Cell Types by Parallel Capsid Screening

2021-09-02

Abstract excerpt

Human brain cells generated by in vitro cell programming provide exciting prospects for disease modeling, drug discovery and cell therapy. These applications frequently require efficient and clinically compliant tools for genetic modification of the cells. Recombinant Adeno-associated viruses (AAVs) fulfill these prerequisites for a number of reasons, including the availability of a myriad of AAV capsid variants w...

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Literature Corpus work: 982bfb5e-a65a-51e7-978d-eda6be3f5ced
DOI: 10.21203/rs.3.rs-861785/v1

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