Discover Community Create You

Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Unmet challenges in cystic fibrosis treatment with modulators.

Expert review of respiratory medicine - 1 Jan 2024

Corrao Federica, Kelly-Aubert Mairead, Sermet-Gaudelus Isabelle, Semeraro Michaela

Abstract excerpt

INTRODUCTION: 'Highly effective' modulator therapies (HEMTs) have radically changed the Cystic Fibrosis (CF) therapeutic landscape. AREAS COVERED: A comprehensive search strategy was undertaken to assess impact of HEMT in life of pwCF, treatment challenges in specific populations such as very young children, and current knowledge gaps. EXPERT OPINION: HEMTs are prescribed for pwCF with definite genotypes. The...

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to Child
Share to Cystic Fibrosis
Share to Cystic Fibrosis Transmembrane Conductance Regulator

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Share to Genotype

Share to Precision Medicine

Share to Quality of Life

Share to Treatment Outcome

Source

Identifiers

PMID: 38755109
DOI: 10.1080/17476348.2024.2357210

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-07.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Unmet challenges in cystic fibrosis treatment with modulators.PMID 38755109Read ↗

An Update on CFTR Modulators as New Therapies for Cystic Fibrosis.Semantic proximity Read ↗

Considerations for early life genetic therapies in cystic fibrosis.Semantic proximity Read ↗

A new era for people with cystic fibrosis.Semantic proximity Read ↗

Understanding and addressing the needs of people with cystic fibrosis in the era of CFTR modulator therapy.Semantic proximity Read ↗

The revolution of personalized pharmacotherapies for cystic fibrosis: what does the future hold?Semantic proximity Read ↗

Advances in the Cystic Fibrosis Drug Development PipelineSemantic proximity Read ↗

Cystic Fibrosis and Its Management Through Established and Emerging Therapies.Semantic proximity Read ↗

CFTR Modulators: Current Status and Evolving Knowledge.Semantic proximity Read ↗

Current state of CFTR modulators for treatment of Cystic Fibrosis.Semantic proximity Read ↗

The New and Advanced Cystic fibrosis transmembrane conductance regulators Modulators in Children with Cystic Fibrosis: A Narrative Review on Long-Term Outcomes, Recent Advances, and Comparative Insights.Semantic proximity Read ↗

The ageing of people living with cystic fibrosis: what to expect now?Semantic proximity Read ↗

Advances in the diagnosis and treatment of cystic fibrosis.Semantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.