Article
CRISPR/Cas9-mediated gene editing. A promising strategy in hematological disorders.
Cytotherapy - 1 Mar 2023
Ugalde Laura, Fañanas Sara, Torres Raúl, Quintana-Bustamante Oscar, Río Paula
Abstract excerpt
The clustered regularly interspaced short palindromic repeats (CRISPR)/Cas9 system has revolutionized the gene editing field, making it possible to interrupt, insert or replace a sequence of interest with high precision in the human genome. Its easy design and wide applicability open up a variety of therapeutic alternatives for the treatment of genetic diseases. Indeed, very promising approaches for the...
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