Article

Rethinking CF organization of care in the era of highly effective modulator: a nationwide research program HORIZON

2024-03-29

Abstract excerpt

<title>Abstract</title> <p>Highly effective modulator therapy (HEMT) is now available to a wider range of people with cystic fibrosis (pwCF). It has significantly improved short-term clinical outcomes and has the potential to alter the natural history of this fatal genetic disease. If long-term follow-up observational data is required to ensure clinical benefits, it is obvious that it will also change the needs o...

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Literature Corpus work: ef86b7a5-519a-5d13-8b95-dbb090d50072
DOI: 10.21203/rs.3.rs-4149166/v1

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