Article

Comparative in vivo characterization of newly discovered myotropic adeno-associated vectors

2023-09-01

Abstract excerpt

<title>Abstract</title> <p>Background Adeno-associated virus (AAV)-based gene therapy is a promising strategy to cure muscle diseases. However, this strategy is currently confronted with challenges, including a lack of transduction efficiency across the entire muscular system and toxicity resulting from off-target tissue effects. Recently, novel myotropic AAVs named MyoAAVs and AAVMYOs have been discovered using...

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Literature Corpus work: dd378e37-5199-5ff4-8c28-4c5b165212bd
DOI: 10.21203/rs.3.rs-3307667/v1

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