Article

Guiding the willingness to pay for repurposed tiratricol in the treatment of Allan-Herndon-Dudley syndrome using a cost-based-plus pricing framework

2025-06-09

Abstract excerpt

<title>Abstract</title> <p><italic>Background:</italic> Tiratricol, initially marketed as Téatrois®, has been repurposed as an orphan drug for Allan-Herndon-Dudley syndrome, a rare genetic disorder affecting thyroid hormone transport. Despite public contributions in its repurposing, the current marketing authorization holder, Egetis Therapeutics, has projected a price of €63,500–€95,000 per patient per year—signi...

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Literature Corpus work: cbb7da40-a474-5276-90ec-77fa3ccff131
DOI: 10.21203/rs.3.rs-6821620/v1

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