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Applying the Efficiency Frontier to Inform Value-Based Pricing for Gaucher Disease Therapies in Brazil

2025-08-27

Abstract excerpt

<h4>Background: </h4> Gaucher Disease (GD) is a rare genetic disorder characterized by visceral and hematological clinical manifestations. Various therapeutic options are currently available, all associated with high costs to the healthcare system, requiring rigorous economic evaluations to support decisions on the incorporation and pricing of these technologies in the Brazilian Unified Health System (SUS). <h4>O...

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Literature Corpus work
7803e60b-0b16-527d-81c1-2165ef810f47
DOI
10.22541/au.175627445.59661418/v1
Open publication

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