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Article

Shining a light in the black box of orphan drug pricing

1 Jan 2014

Abstract excerpt

BACKGROUND: The pricing mechanism of orphan drugs appears arbitrary and has been referred to as a "black box". Therefore, the aim of this study is to investigate how drug- and disease-specific variables relate to orphan drug prices. Additionally, we aim to explore if certain country-specific pricing and reimbursement policies affect the price level of orphan drugs. METHODS: Annual treatment costs per indication...

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Identifiers

PMID: 24767472
DOI: 10.1186/1750-1172-9-62

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