Article

Curative Approach to the Treatment of Beta-Thalassemia and Sickle Cell Disease with Hematopoietic Stem Cell Transplantation

2025-12-31

Abstract excerpt

b-thalassemia and sickle cell disease are two inherited hematological diseases due to defective hemoglobin synthesis or to the production of hemoglobin with altered properties. These two conditions have prolonged survival with modern support therapies, albeit life-long, complex, expensive and resources-consuming. Studies carried out in the last three decades have shown that allogeneic hematopoietic stem cell trans...

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Literature Corpus work: c199f64e-9e5b-5167-9c04-05d3869c302b
DOI: 10.20944/preprints202512.2672.v1

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