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Article

Gene therapy for hemoglobinopathies: progress and challenges.

Translational research : the journal of laboratory and clinical medicine - 1 Apr 2013

Dong Alisa, Rivella Stefano, Breda Laura

Abstract excerpt

Hemoglobinopathies are genetic inherited conditions that originate from the lack or malfunction of the hemoglobin (Hb) protein. Sickle cell disease (SCD) and thalassemia are the most common forms of these conditions. The severe anemia combined with complications that arise in the most affected pa...

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Identifiers

PMID: 23337292
DOI: 10.1016/j.trsl.2012.12.011
PMCID: PMC3716457

Genes

SCD

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 4 Sept 2026. Prepared record publication-23337292-2026-09-04.2. Manifest publication-graph-cohort-2026-09-04.2.

Source receipt: PubMed via Helena Literature Corpus, retrieved 4 Sept 2026.

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