Article

Patient-reported impact of Charcot-Marie-Tooth disease: protocol for a real-world digital lifestyle study

2020-10-28

Abstract excerpt

<title>Abstract</title> <p>Background Charcot-Marie-Tooth disease (CMT) is a rare, chronic, progressive motor and sensory neuropathy that affects the peripheral nervous system, leading to progressive, predominantly distal muscle weakness, atrophy, sensory loss and progressive limb dysfunction. As with many rare diseases, there is a lack of patient-reported data with which to understand and address patient needs....

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Literature Corpus work: b1ea19f9-1a6b-5bf8-aeb5-14aedf5d0977
DOI: 10.21203/rs.3.rs-36305/v2

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