Article

Spinal Muscular Atrophy: The High Costs of Innovative Therapies for Rare Diseases

2021-02-23

Abstract excerpt

<title>Abstract</title> <p><bold>Background:</bold> Despite numbers of prescriptions filled remaining constant, expenditures for drugs are rising. Among others, this is caused by high prices for orphan drugs and advanced therapy medicinal products (ATMPs). Despite attempts by policymakers to intervene, the increasing use of these therapies poses numerous challenges on the health care system.<bold>Results:</bold>...

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Literature Corpus work: d8a392c2-c529-51ca-9ff7-993f7a958aa2
DOI: 10.21203/rs.3.rs-236540/v1

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