Article

A Framework for Inclusive and Accessible Clinical Research in Rare Diseases

2025-05-08

Abstract excerpt

<h4>Background</h4> Equitable representation of all populations is crucial for generalizing rare disease (RD) clinical research outcomes, especially given the low prevalence and geographically sparse distribution of patients with RDs. In our companion manuscript ( Current State and Demographic Trends of Medically Underserved Populations in Rare Disease Research , Manjunatha et al. ) we quantified reporting of demo...

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Literature Corpus work: 72d4fe61-ffe2-51b9-abce-ac062c909623
DOI: 10.1101/2025.05.07.25326565

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