Article

Cardiac Cell and Animal Models for Duchenne Muscular Dystrophy in the Era of Gene Therapy and Precision Medicine

2025-08-01

Abstract excerpt

Duchenne muscular dystrophy (DMD) is a lethal inherited muscle disease caused by mutations in the DMD gene, and the development of gene therapies targeting DMD is rapidly progressing. Patient-derived induced pluripotent stem cells and animal models that mimic patient-specific mutations have significantly contributed to the advancement of precision medicine based on individual genetic profiles. Currently, no diseas...

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Literature Corpus work: 709ae932-6759-5485-8a12-db57feb1ae05
DOI: 10.20944/preprints202508.0032.v1

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