Article

A Single Lipid Nanoparticle Formulation Enables Delivery of Diverse RNA Therapeutics to Human Muscle Models of Duchenne Muscular Dystrophy

2026-07-29

Abstract excerpt

<h4>ABSTRACT</h4> Duchenne muscular dystrophy is a lethal neuromuscular disorder caused by the absence of dystrophin, for which no curative treatment is available. RNA-based approaches have shown promising results; however, their evaluation is hindered by the lack of robust and rapid delivery methods for differentiated human muscle cells, which represent the most physiologically relevant in vitro models for asse...

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Literature Corpus work: 6ae2cfa8-9e60-529f-b81a-81e2d87e4919
DOI: 10.64898/2026.07.29.741396

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