Article

Advances in RNA Therapeutics: Classes, Innovations and Clinical Applications

2025-04-10

Abstract excerpt

RNA therapeutics represent a transformative class of treatments capable of correcting genetic errors, modulating gene expression, and enabling targeted intervention across a wide range of diseases. These platforms—including antisense oligonucleotides (ASOs), small interfering RNAs (siRNAs), messenger RNAs (mRNAs), and microRNAs (miRNAs)—have progressed from proof-of-concept to clinical reality, with multiple FDA-a...

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Literature Corpus work: 269c2d08-1700-5205-8427-6a78b239b365
DOI: 10.20944/preprints202504.0866.v1

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