Article

Design Strategies of Adeno-Associated Virus (AAV) Vectors in Gene Therapy

2024-01-31

Abstract excerpt

Adeno-associated viruses (AAV) have attracted significant attention in the field of gene and cell therapy due to highly effective delivery of therapeutic genes into human cells. At present, three AAV-based gene therapy drugs (Glybera, Luxturna and Zolgensma) for the treatment of genetic diseases have been approved by the European Medicines Agency (EMA) and the U.S Food and Drug Administration (FDA) during 2012-202...

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Literature Corpus work: 4eb25aad-b07d-55de-83be-b73db3931e64
DOI: 10.22541/au.170669894.49564813/v1

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