Article

Collaboration for rare disease drug discovery research

2014-10-31

Abstract excerpt

Rare disease research has reached a tipping point, with the confluence of scientific and technologic developments that if appropriately harnessed, could lead to key breakthroughs and treatments for this set of devastating disorders. Industry-wide trends have revealed that the traditional drug discovery research and development (R&D) model is no longer viable, and drug companies are evolving their approach. Rather...

Topics

Open a Topic to create a Post that cites this publication.

Identifiers and source

Literature Corpus work: 46f849bb-d629-543a-a0f2-b30f49063473
DOI: 10.12688/f1000research.5564.1

Open publication

Related research

Semantic proximity does not establish scientific evidence.

Click a neighbor to travelStep 1 · 12 closest

Collaboration for rare disease drug discovery researchDOI 10.12688/f1000research.5564.1Read

The future of Rare Disease Drug development: the Rare Disease Cures Accelerator Data Analytics Platform (RDCA-DAP)Semantic proximity Read

The rare-to-common disease journey: a winding road to new therapies.Semantic proximity Read

Patients with rare diseases: from therapeutic orphans to pioneers of personalized treatments.Semantic proximity Read

Rare Diseases Clinical Trials Toolbox - Public resources and main considerations to set up a clinical trial on medicinal products for humans in EuropeSemantic proximity Read

ModelMatcher: A scientist-centric online platform to facilitate collaborations between stakeholders of rare and undiagnosed disease researchSemantic proximity Read

RaDiCo, the French National Program on Rare Disease CohortsSemantic proximity Read

Data sharing in the undiagnosed diseases network.Semantic proximity Read

Quantifying hope: An EU perspective of rare disease therapeutic space and market dynamicsSemantic proximity Read

Recommendations from the IRDiRC Working Group on methodologies to assess the impact of diagnoses and therapies on rare disease patientsSemantic proximity Read

Genomics4RD: An integrated platform to share Canadian deep-phenotype and multiomic data for international rare disease gene discovery.Semantic proximity Read

Clinical research challenges in rare genetic diseases in BrazilSemantic proximity Read

An interconnected data infrastructure to support large-scale rare disease research.Semantic proximity Read