Article

The future of Rare Disease Drug development: the Rare Disease Cures Accelerator Data Analytics Platform (RDCA-DAP)

2023-01-06

Abstract excerpt

Rare disease drug development is wrought with challenges not the least of which is access to the limited data currently available throughout the rare disease ecosystem where sharing of the available data is not guaranteed. Most pharmaceutical sponsors seeking to develop agents to treat rare diseases will initiate data landscaping efforts to identify various data sources that might be informative with respect to di...

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Literature Corpus work: dfb5543c-1bd1-5066-880c-4c575e36d9cf
DOI: 10.21203/rs.3.rs-2431930/v1

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