Article

Rare Diseases Clinical Trials Toolbox - Public resources and main considerations to set up a clinical trial on medicinal products for humans in Europe

2024-02-17

Abstract excerpt

<h4>Background</h4> Drug development programmes in rare diseases have many challenges, some of which differ from those facing researchers working on common diseases, like the scarcity of patients. Over the past years, research and regulatory initiatives, as well as resources have been implemented to expedite drug development for rare diseases. Nevertheless, these tools have been developed in the context of differe...

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Literature Corpus work: 5aab7ff0-f3b2-5db2-a013-daae798b193f
DOI: 10.1101/2024.02.15.24302854

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