Article

Clinical outcome evaluations and CBT response prediction in Myotonic Dystrophy

2021-03-01

Abstract excerpt

<h4>Background</h4> The European OPTIMISTIC clinical trial has demonstrated a significant, yet heterogenous effect of Cognitive Behavioural Therapy (CBT) for Myotonic Dystrophy type 1 (DM1) patients. One of its remaining aims was the assessment of efficacy and adequacy of clinical outcome measures, including the relatively novel primary trial outcome, the DM1-Activ-c questionnaire. <h4>Objectives</h4> Assessment o...

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Literature Corpus work: 0bdae4f0-95c7-5b56-b2eb-68c2b743bbd3
DOI: 10.1101/2021.02.25.21252140

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