Article
Validation of the North Star Assessment for Limb-Girdle Type Muscular Dystrophies.
Physical therapy - 6 Oct 2022
James Meredith K, Alfano Lindsay N, Muni-Lofra Robert, Reash Natalie F, Sodhi Jassi, Iammarino Megan A, Moat Dionne, Shannon Kianna, McCallum Michelle, Richardson Mark, Eagle Michelle, Straub Volker, Marini-Bettolo Chiara, Lowes Linda P, Mayhew Anna G
Abstract excerpt
OBJECTIVE: The North Star Assessment for limb-girdle type muscular dystrophies (NSAD), a clinician-reported outcome measure (ClinRO) of motor performance, was initially developed and validated for use in dysferlinopathy, an autosomal recessive form of limb-girdle muscular dystrophy (LGMD R2/2B). Recent developments in treatments for limb-girdle muscular dystrophies (LGMD) have highlighted the urgent need for...
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