Voretigene Neparvovec and Gene Therapy for Leber’s Congenital Amaurosis: Review of Evidence to Date

Abstract excerpt

Abstract: Gene therapy has now evolved as the upcoming modality for management of many disorders, both inheritable and non-inheritable. Knowledge of genetics pertaining to a disease has therefore become paramount for physicians across most specialities. Inheritable retinal dystrophies (IRDs) are notorious for progressive and relentless vision loss, frequently culminating in complete blindness in both eyes....

Topics

Share this publication in a Topic to start or enrich a Post.

• Share to Ocular Disorders and Treatments
• Share to Retinal and Macular Surgery
• Share to Retinal Development and Disorders