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Article

Retinal gene therapy

12 Feb 2018

Abstract excerpt

Introduction: Inherited retinal diseases are the leading cause of sight impairment in people of working age in England and Wales, and the second commonest in childhood. Gene therapy offers the potential for benefit. Sources of data: Pubmed and clinicaltrials.gov. Areas of agreement: Gene therapy can improve vision in RPE65-associated Leber Congenital Amaurosis (RPE65-LCA). Potential benefit depends on efficient...

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Identifiers

PMID: 29506236
DOI: 10.1093/bmb/ldy005

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026.

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